Together with Dr. Aijun Wang we are working to design and test a therapy targeting the UBE3A gene-the overexpression of which leads to Dup15q syndrome. Patients with Dup15q syndrome are chronically ill with significant intellectual disability, ASD, and many experience epilepsy.
For more read: https://health.ucdavis.edu/mind-institute/news/headlines/dream-team-to-develop-in-utero-gene-editing-therapy-for-a-rare-neurological-genetic-disorder/2025/09
For more on Dup15q vist: https://dup15q.org/understanding-dup15q-syndrome/